Adults with hemophilia B saw their number of bleeding episodes drop by an average of 71% after a single infusion of gene therapy, according to the results of an international Phase III clinical trial published in the New England Journal of Medicine by researchers from the University of Pennsylvania Perelman School of Medicine and a...
Tag: <span>hemophilia B</span>
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Gene therapy more cost effective than current treatments for hemophilia B
by St. Jude Children’s Research Hospital Credit: CC0 Public Domain A St. Jude Children’s Research Hospital analysis found a major gap between the cost to manufacture and distribute hemophilia B gene therapy and the $2 million-plus price reportedly under consideration for hemophilia gene therapy now in development. The study appeared online in the journal Blood. It is the first to report gene...
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Hemophilia three times more prevalent than thought
by Veronica Mcguire, McMaster University More than 1,125,000 men around the world have the inherited bleeding disorder of hemophilia, and 418,000 of those have a severe version of the mostly undiagnosed disease, says a new study led by McMaster University researchers. This is three times what was previously known. Only 400,000 people globally were estimated to have the disorder which is caused...