Preferential regeneration of oxidative myofibers in DMD muscles after cell transplantation. Credit: Stem Cell Research & Therapy (2024). Duchenne muscular dystrophy (DMD) is a neuromuscular disease causing progressive skeletal muscle weakness and fatigue. The research team led by Associate Professor Hidetoshi Sakurai (Department of Clinical Application), Researcher Nana Takenaka-Ninagawa, and graduate student Clémence Kiho Yoshioka recently demonstrated...
Tag: <span>Duchenne muscular dystrophy (DMD)</span>
Post
Dogs with Duchenne Treated with Gene Therapy
Like humans, some golden retrievers develop Duchenne muscular dystrophy (DMD), a hereditary muscle wasting condition that begins early in life. Using gene therapy, scientists were able to restore muscle function in dogs with the disease, according to a study published today (July 25) in Nature Communications. Researchers injected microdystrophin, a shortened version of the dystrophin gene that individuals with...