Jim Kling PHOENIX – New therapies are on the horizon for genetic neuromuscular diseases, and this will raise both hopes for patients and challenges for neurologists. Following successful genetic treatments for ALS, hereditary amyloidosis, and spinal muscular atrophy, therapies for conditions like Charcot-Marie-Tooth (CMT) neuropathy are set to change neurology practice, according to Nicolas Madigan,...
Tag: <span>Genetic Therapies</span>
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Genetic Therapies for Brain Diseases
By Diana Kwon, Nature magazine on May 13, 2021 Evie Lewis with her parents, Elliot and Janell. Evie receives a dose of a genetic therapy every few months to treat spinal muscular atrophy. Credit: Kim Raff Nature Susan was still a child when she first suspected something might be wrong with her mother. A cup or plate would often crash...