A new form of therapy may halt or even reverse a form of progressive vision loss that, until now, has inevitably led to blindness. This hyper-targeted approach offers hope to individuals living with spinocerebellar ataxia type 7 (SCA7) and validates a new form of therapy with the potential to treat neurogenetic diseases effectively and with...
Tag: <span>ataxin 2 protein</span>
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Suppressing single protein greatly extends life span of mice with ALS-like disease
A set of experiments at Stanford reveals that suppressing a protein called ataxin 2 dramatically extends survival and improves motor function in a mouse model of ALS. Aaron Gitler and his colleagues found that suppressing a protein in mice genetically engineered to have an ALS-like disease allowed them to live longer and improved their motor...