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Mouse study shows gene therapy may correct creatine deficiency disorder
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Mouse study shows gene therapy may correct creatine deficiency disorder

by University of California, Los Angeles Credit: CC0 Public Domain A new study in mice finds that a gene therapy developed by a UCLA researcher appears to correct a rare creatine deficiency disorder that commonly results in intellectual disabilities, problems with speech, involuntary movements and recurrent seizures. The treatment potentially could represent an improvement upon...