Tag: <span>dwarfism</span>

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Bone growth drug may reduce sudden infant death syndrome in children with common form of dwarfism

Peer-Reviewed Publication MURDOCH CHILDRENS RESEARCH INSTITUTE A drug that boosts bone growth in children with the most common form of dwarfism, may also reduce their chances of sudden infant death syndrome, sleep apnoea and needing surgery, according to a new study. The international research trial, led by Murdoch Children’s Research Institute (MCRI) and published in...

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FDA opens up an ethical can of worms with accelerated approval for first drug for underlying genetic cause of dwarfism

Jean-Jacques Bienaimé (BioMarin via Youtube) November 19, 2021 11:10 AM EST FDA+ FDA opens up an ethical can of worms with accelerated approval for first drug for underlying genetic cause of dwarfism. The FDA on Friday signed off on an accelerated approval for Biomarin’s Voxzogo (vosoritide) injection, the first treatment to target the underlying genetics...