Tag: <span>Gene Silencer</span>

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Injection of Virus-Delivered Gene Silencer Blocks ALS Degeneration, Saves Motor Function

Writing in Nature Medicine, an international team headed by researchers at University of California San Diego School of Medicine describe a new way to effectively deliver a gene-silencing vector to adult amyotrophic lateral sclerosis (ALS) mice, resulting in long-term suppression of the degenerative motor neuron disorder if treatment vector is delivered prior to disease onset,...