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A milestone in muscular dystrophy therapy
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A milestone in muscular dystrophy therapy

MAX DELBRÜCK CENTER FOR MOLECULAR MEDICINE IN THE HELMHOLTZ ASSOCIATION IMAGE: THE CONFOCAL MICROSCOPE IMAGE SHOWS THE PATIENT’S PRIMARY MUSCLE STEM CELLS, WHICH HAVE CONTINUED TO PROLIFERATE AFTER REPAIR OF THE MUTATION USING “BASE EDITING “. CREDIT: SPULER LAB, ECRC Muscle stem cells enable our muscle to build up and regenerate over a lifetime through...