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Genethon announces publication of results paving the way for gene therapy for XLH, a skeletal disorder

AFM-TÉLÉTHON PARIS, FRANCE (November xx, 2021) – Genethon, a unique non-profit gene therapy R&D organization founded by the French Muscular Dystrophy Association (AFM-Telethon), announced today publication in the open-access journal Science Advances of research describing advances in using AAV-based gene therapy for potential long-lasting treatment of X-linked hypophosphatemia (XLH), a serious skeletal disease caused by low levels of phosphate...