August 29, 2024 by University of Hawaii at Manoa Graphical abstract. Credit: Nucleic Acids Research (2024). DOI: 10.1093/nar/gkae534For decades, scientists have dreamed of a future where genetic diseases, such as the blood clotting disorder hemophilia, could be a thing of the past. Gene therapy, the idea of fixing faulty genes with healthy ones, has held...